Wave Life Sciences (NASDAQ:WVE) is one of the 17 biotechnology stocks with more than 50% upside. As of the February 12 ...
A multinational, multidisciplinary group of experts has created a consensus document to guide diagnosis, staging and management of adults with alpha-1 antitrypsin deficiency-associated liver disease, ...
TSRA-196 is designed to precisely correct the genetic mutation underlying AATD, with the goal of restoring production of functional alpha-1 antitrypsin (AAT) protein through a one-time, durable ...
New registry data show bronchiectasis affects multiple alpha-1 antitrypsin deficiency genotypes, not just Pi*ZZ.
YolTech Therapeutics, a late clinical-stage biotechnology company developing in vivo gene editing therapies, today announced ...
Alpha-1-antitrypsin is a so-called protease inhibitor, a type of enzyme inhibitor. It is produced in the liver but exerts its effects in the lungs, where it regulates immune cell activity. This ...
Patients with lung disease are more likely to develop heart disease independent of any risk factors, according to new research. Boosting levels of a deficient protein has clear survival benefits for ...
Austin, Texas, Jan. 13, 2026 (GLOBE NEWSWIRE) -- Alpha-1 Antitrypsin Deficiency Market Size & Growth Analysis: According to SNS Insider, The Alpha-1 Antitrypsin Deficiency Market was valued at USD ...
“The FDA’s orphan drug designation is an important milestone in our development plan for DCR-A1AT for alpha-1 antitrypsin deficiency-associated liver disease and underscores the treatment need that ...
Alpha-1 antitrypsin deficiency (AATD) is an inherited genetic disorder. It can occur in anyone but is more common in people with ancestry in North and Central Europe. People with AATD experience ...
Please provide your email address to receive an email when new articles are posted on . Direct-to-consumer testing, combined with clinical follow-up, helped identify patients with undiagnosed alpha-1 ...
Early emphysema due to alpha 1-antitrypsin deficiency (alpha 1-ATD) in a young patient with asthma is an unusual and frequently missed diagnosis. Theoretical and clinical evidence supports the ...