The federal approval of two new gene therapy treatments for sickle cell disease has created a groundbreaking option for patients. Across the nation, it is unknown how many suffer from the disease, but ...

A class of drugs used for their ability to stop tumor cells from dividing is now under study for their potential to reduce the pain and damage caused by sickle cell disease, investigators report. The ...

Sickle cell thalassemia occurs when you inherit both a sickle cell gene mutation and a thalassemia gene mutation. Symptoms are similar to other types of sickle cell disease but can vary depending on ...

Sickle cell disease (SCD) is a genetic disorder that affects millions of people worldwide. The disease is caused by a mutation in the hemoglobin gene, which leads to the formation of abnormal ...

WASHINGTON — The only cure for painful sickle cell disease today is a bone marrow transplant. But soon there may be a new cure that attacks the disorder at its genetic source. On Tuesday, advisers to ...

The U.S. Food and Drug Administration on Friday approved two gene-based treatments for sickle cell disease, including the first therapy that uses the gene-editing technique CRISPR, opening a new era ...

(CNN) — Before Johnny Lubin got a potentially life-changing experimental treatment at the age of 13, he recalls, he had one main concern. “I was worrying that I might get, like, superpowers,” said ...

Sickle cell anemia is an inherited condition that impacts red blood cells. It can cause a variety of symptoms, which may include anemia, infections, and blockages in blood vessels. Sickle cell disease ...

I am a carrier for the sickle cell gene. My A1C has been slightly elevated for years. I would like to know if having the sickle cell trait affects the results of an A1C. -- P.S. ANSWER: Having the ...

Fulcrum Therapeutics (NASDAQ:FULC) fell ~10% on Tuesday after the company posted data from a late-stage study of its lead candidate, Pociredir, in sickle cell disease, along with second quarter ...